Startups, BioPharma

Gene therapy player Audentes Therapeutics raises $65M

Audentes Therapeutics, a San Francisco-based gene therapy startup, just raised $65 million to advance three candidates to the clinic that treat X-linked myotubular myopathy, Pompe disease and a rare form of tachycardia called CPVT.

Bay Area gene therapy startup Audentes Therapeutics just closed out an oversubscribed Series C round of $65 million.

Audentes is developing adeno-associated virus-based therapeutics that inject disease-correcting genes into a patient’s cells. It’s focusing on three diseases: X-linked myotubular myopathy, Pompe disease and a rare form of tachycardia called CPVT. While they’re all preclinical, the new influx of funding will advance these three candidates into the clinic, Audentes says.

The company has well-established relationships with patient groups associated with these diseases, which should help Audentes hasten the clinical trial recruitment process. It has also set up a patient advocacy website

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The round was led by existing investor Sofinnova Ventures and new investor Redmiel Group. Other participants include RA Capital Management, OrbiMed, 5AM Ventures, Versant Ventures, Deerfield Management and Venrock.

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